Search results for: Marc F. Botteman

Items from 1 to 20 out of 24 results

article

Epidemiological and clinical characteristics of symptomatic hereditary transthyretin amyloid polyneuropathy: a global case series

Márcia Waddington-Cruz, Hartmut Schmidt, Marc F. Botteman, John A. Carter, more

Orphanet Journal of Rare Diseases > 2019 > 14 > 1 > 1-7

We describe 542 cases of symptomatic hereditary transthyretin amyloid polyneuropathy (ATTR-PN) identified through a review of the literature published between 2005 and 2016. Approximately 18% of the cases were from countries where ATTR-PN is traditionally considered to be endemic (i.e., Portugal, Japan, and Sweden). East Asia (Japan, China, Taiwan, and South Korea) contributed a sizeable combined...

article

Estimating the global prevalence of transthyretin familial amyloid polyneuropathy

Hartmut H. Schmidt, Márcia Waddington‐Cruz, Marc F. Botteman, John A. Carter, more

Muscle & Nerve > 57 > 5 > 829 - 837

Introduction: This study sought to estimate the global prevalence of transthyretin familial amyloid polyneuropathy (ATTR‐FAP). Methods: Prevalence estimates and information supporting prevalence calculations was extracted from records yielded by reference‐database searches (2005–2016), conference proceedings, and nonpeer reviewed sources. Prevalence was calculated as prevalence rate multiplied by...

article

Understanding the Disease Course and Therapeutic Benefit of Tafamidis Across Real-World Studies of Hereditary Transthyretin Amyloidosis with Polyneuropathy: A Proof of Concept for Integrative Data Analytic Approaches

Daniel Serrano, Christopher B. Atzinger, Marc F. Botteman

Neurology and Therapy > 2018 > 7 > 1 > 141-154

Introduction Hereditary transthyretin (TTR) amyloidosis with polyneuropathy (hATTR-PN) is a rare, autosomal dominant amyloidosis characterized primarily by progressive ascending sensorimotor neuropathy often associated with autonomic involvement. hATTR-PN is caused by a mutation in the TTR gene leading to protein misfolding and amyloid accumulation in peripheral nerves and vital organs. The latest...

article

Estimating Population-Level Prevalence of Wild-Type and Variant Transthyretin Amyloid Cardiomyopathy

Martha Grogan, Fabian Aus dem Siepen, John A. Carter, Marc F. Botteman, more

Journal of Cardiac Failure > 2017 > 23 > 8(S) > S73

article

Economic Burden of Atopic Dermatitis in High-Risk Infants Receiving Cow's Milk or Partially Hydrolyzed 100% Whey-Based Formula

Abhijeet Bhanegaonkar, Erica G. Horodniceanu, Xiang Ji, Patrick Detzel, more

The Journal of Pediatrics > 2015 > 166 > 5 > 1145-1151.e3

To estimate the health and economic impact of feeding partially hydrolyzed formula–whey (PHF-W) instead of standard cow's milk formula (CMF) for the first 4 months of life among US infants at high risk for developing atopic dermatitis (AD).A Markov model was developed integrating published data, a survey of US pediatricians, costing sources and market data, and expert opinion. Key modeled outcomes...

article

Cost-Effectiveness of Partially Hydrolyzed Whey Protein Formula in the Primary Prevention of Atopic Dermatitis in At-Risk Urban Filipino Infants

Abhijeet J. Bhanegaonkar, Erica G. Horodniceanu, Rizalina Racquel H. Gonzalez, Maria Victoria Canlas Dizon, more

Value in Health Regional Issues > 2014 > 3 > Complete > 124-135

To estimate, from a Filipino societal perspective, the cost-effectiveness of preventing atopic dermatitis (AD) via early nutritional intervention with 100% whey-based partially hydrolyzed formula (PHF-W) versus standard cow’s milk formula (SF) in healthy, urban infants with atopic heredity who are not exclusively breast-fed.A Markov model was used to simulate over 6 years the incidence of AD, days...

article

Patterns of Clinical Management of Atopic Dermatitis in Infants and Toddlers: A Survey of Three Physician Specialties in the United States

José M. Saavedra, Mark Boguniewicz, Sarah Chamlin, Alan Lake, more

The Journal of Pediatrics > 2013 > 163 > 6 > 1747-1753

To describe atopic dermatitis (AD) management patterns in children ≤36 months old as reported by pediatricians, dermatologists, and allergists in the US.A nationally-representative survey was administered to pediatricians (n = 101), dermatologists (n = 26), and allergists (n = 26). Main outcomes included referrals to health care professionals, suggested/ordered laboratory tests, management approach...

article

The impact of second-line agents on patients’ health-related quality of life in the treatment for non-small cell lung cancer: a systematic review

Arijit Ganguli, Phillip Wiegand, Xin Gao, John A. Carter, more

Quality of Life Research > 2013 > 22 > 5 > 1015-1026

Purpose In advanced non-small cell lung cancer (NSCLC), progressive disease burdens patients considerably. Second-line (2L) chemotherapy improves survival marginally but humanistic outcomes (i.e., quality of life, QOL) are underreported. The impact of 2L therapy remains an important consideration for patients and caregivers, and there have been QOL reviews for 1L, but not 2L, therapies. This review...

article

Cost-Effectiveness of Denosumab Versus Zoledronic Acid in the Management of Skeletal Metastases Secondary to Breast Cancer

Sonya J. Snedecor, John A. Carter, Satyin Kaura, Marc F. Botteman

Clinical Therapeutics > 2012 > 34 > 6 > 1334-1349

Denosumab has been approved in the United States for the prevention of skeletal-related events (SREs) in metastatic breast cancer. In a Phase III trial in patients with bone-metastatic breast cancer (N = 2033), denosumab was associated with a significantly delayed time to first SRE (by 18%; P < 0.001 noninferiority; P = 0.01 superiority) and time to first and subsequent SREs (by 23%; P = 0.001)...

article

Pharmacoeconomics of Bisphosphonates for Skeletal-Related Event Prevention in Metastatic Non-Breast Solid Tumours

John A. Carter, Avani D. Joshi, Satyin Kaura, Marc F. Botteman

PharmacoEconomics > 2012 > 30 > 5 > 373-386

Bisphosphonates reduce the risk of skeletal-related events (SREs; i.e. spinal cord compression, pathological fracture, radiation or surgery to the bone, and hypercalcaemia) in patients with metastatic cancer. A number of analyses have been conducted to assess the cost effectiveness of bisphosphonates in patients with bone metastases secondary to breast cancer, but few in other solid tumours. This...

article

Estimating Preference-Based EQ-5D Health State Utilities or Item Responses from Neuropathic Pain Scores

Ning Yan Gu, Chris Bell, Marc F. Botteman, Xiang Ji, more

The Patient - Patient-Centered Outcomes Research > 2012 > 5 > 3 > 185-197

Background Preference-based health state utilities are required for many health economic evaluations. When the direct evidence of such is lacking and only condition-specific scores are available, establishing a ‘mapping’ relationship between instruments can be useful. Objective Our objective was to map the 11-point Pain Intensity Numerical Rating Scale (PI-NRS-11), a pain-specific instrument ranging...

article

Cost-Effectiveness of Zoledronic Acid in the Management of Skeletal Metastases in Patients With Lung Cancer in France, Germany, Portugal, The Netherlands, and the United Kingdom

Avani D. Joshi, John A. Carter, Marc F. Botteman, Satyin Kaura

Clinical Therapeutics > 2011 > 33 > 3 > 291-304.e8

Zoledronic acid (ZOL) significantly reduces the risk of new skeletal-related events (SREs) in patients with non–small cell lung cancer (NSCLC) who have bone metastases.The purpose of this study was to assess the cost and cost-effectiveness of ZOL in the management of skeletal metastases in this population across 5 European countries (France, Germany, United Kingdom, Portugal, and the Netherlands)...

article

Transmission-dynamic model to capture the indirect effects of infant vaccination with Prevnar (7-valent pneumococcal conjugate vaccine (PCV7)) in older populations

Sonya J. Snedecor, David R. Strutton, Vincent Ciuryla, Elissa J. Schwartz, more

Vaccine > 2009 > 27 > 34 > 4694-4703

We developed an age-structured, transmission-dynamic, mathematical model to quantify the direct and indirect benefits of infant PCV7 vaccination. The model simulates the acquisition of asymptomatic carriage of Streptococcus pneumoniae and the development of fatal and non-fatal invasive pneumococcal disease (IPD) among vaccinated and unvaccinated individuals aged <2, 2–4, 5–17, 18–49, 50–64, and...

article

ZOLEDRONIC ACID IS COST EFFECTIVE FOR THE PREVENTION OF SKELETAL-RELATED EVENTS IN PATIENTS WITH PROSTATE CANCER AND BONE METASTASES IN FRANCE AND GERMANY

Marjan Meijboom, Marc F Botteman, Satyin Kaura

The Journal of Urology > 2009 > 181 > 4 Supplement > 295

article

ZOLEDRONIC ACID IS COST EFFECTIVE FOR THE PREVENTION OF SKELETAL-RELATED EVENTS IN PATIENTS WITH BONE METASTASES FROM RENAL CELL CARCINOMA: A FRENCH EXPLORATORY ANALYSIS

Marc F Botteman, Jennifer M Stephens, Isaac Foley, Satyin Kaura

The Journal of Urology > 2009 > 181 > 4 Supplement > 500

article

S165 – Locally Advanced Head and Neck Cancer Treatment Patterns

Wildon R. Farwell, Elizabeth Lawler, Subha Chittamooru, Marc F. Botteman

Otolaryngology - Head and Neck Surgery > 2008 > 139 > 2 Supplement 1 > P131

article

Preferences and Utilities of Health Outcomes and Treatments Associated with Head and Neck Cancer

Yoko Komatsuzaki, Paola Gramegna, Jennifer M. Stephens, Marc F. Botteman, more

American Journal of Cancer > 2006 > 5 > 1 > 27-34

As a result of increased patient knowledge and autonomy, patient input into treatment decisions is becoming more acceptable and common. The outcomes of treatments for cancers of the oral cavity, pharynx, and larynx, collectively known as head and neck cancer (HNC), vary. Knowing how patients value the outcomes of alternative treatments for HNC may be useful to physicians and healthcare providers in...

article

Economic burden of acute myeloid leukemia: a literature review

Alberto Redaelli, Marc F. Botteman, Jennifer M. Stephens, Suzanne Brandt, more

Cancer Treatment Reviews > 2004 > 30 > 3 > 237-247

Objective: The primary objective was to examine the economic burden associated with acute myeloid leukemia (AML), a deadly hematological malignancy. AML is the most common form of acute leukemia in adults, particularly in individuals over 60 years of age; AML also accounts for 15-20% of childhood leukemia.Materials and methods: A systematic review was conducted of relevant studies published in the...

article

Short- and long-term effects of acute myeloid leukemia on patient health-related quality of life

Alberto Redaelli, Jennifer M. Stephens, Suzanne Brandt, Marc F. Botteman, more

Cancer Treatment Reviews > 2004 > 30 > 1 > 103-117

Objectives: Patients with acute myeloid leukemia (AML) may receive aggressive therapies (e.g., chemotherapy and bone marrow transplantation (BMT)) that are thought to significantly affect HRQL. Therefore, the goal of this study was to assess the HRQL impact on patients of AML and its treatments.Materials and methods: An electronically assisted literature survey and synthesis was conducted of English-language...

article

Economic burden of head and neck cancerA literature review

Jennifer M. Lee, Marco Turini, Marc F. Botteman, Jennifer M. Stephens, more

The European Journal of Health Economics > 2004 > 5 > 1 > 70-80

This literature review presents the economics of head and neck cancer (HNC), the worlds sixth most common neoplasm. HNC economics is complicated by the involvement of multiple body sites, multiple medical specialties, and multiple treatment modalities. Economic analyses of HNC published in English between 1990 and 2002 were identified from electronic data sources. Additional studies were identified...

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INFONA - science communication portal

Search results for: Marc F. Botteman

Epidemiological and clinical characteristics of symptomatic hereditary transthyretin amyloid polyneuropathy: a global case series

Estimating the global prevalence of transthyretin familial amyloid polyneuropathy

Understanding the Disease Course and Therapeutic Benefit of Tafamidis Across Real-World Studies of Hereditary Transthyretin Amyloidosis with Polyneuropathy: A Proof of Concept for Integrative Data Analytic Approaches

Estimating Population-Level Prevalence of Wild-Type and Variant Transthyretin Amyloid Cardiomyopathy

Economic Burden of Atopic Dermatitis in High-Risk Infants Receiving Cow's Milk or Partially Hydrolyzed 100% Whey-Based Formula

Cost-Effectiveness of Partially Hydrolyzed Whey Protein Formula in the Primary Prevention of Atopic Dermatitis in At-Risk Urban Filipino Infants

Patterns of Clinical Management of Atopic Dermatitis in Infants and Toddlers: A Survey of Three Physician Specialties in the United States

The impact of second-line agents on patients’ health-related quality of life in the treatment for non-small cell lung cancer: a systematic review

Cost-Effectiveness of Denosumab Versus Zoledronic Acid in the Management of Skeletal Metastases Secondary to Breast Cancer

Pharmacoeconomics of Bisphosphonates for Skeletal-Related Event Prevention in Metastatic Non-Breast Solid Tumours

Estimating Preference-Based EQ-5D Health State Utilities or Item Responses from Neuropathic Pain Scores

Cost-Effectiveness of Zoledronic Acid in the Management of Skeletal Metastases in Patients With Lung Cancer in France, Germany, Portugal, The Netherlands, and the United Kingdom

Transmission-dynamic model to capture the indirect effects of infant vaccination with Prevnar (7-valent pneumococcal conjugate vaccine (PCV7)) in older populations

ZOLEDRONIC ACID IS COST EFFECTIVE FOR THE PREVENTION OF SKELETAL-RELATED EVENTS IN PATIENTS WITH PROSTATE CANCER AND BONE METASTASES IN FRANCE AND GERMANY

ZOLEDRONIC ACID IS COST EFFECTIVE FOR THE PREVENTION OF SKELETAL-RELATED EVENTS IN PATIENTS WITH BONE METASTASES FROM RENAL CELL CARCINOMA: A FRENCH EXPLORATORY ANALYSIS

S165 – Locally Advanced Head and Neck Cancer Treatment Patterns

Preferences and Utilities of Health Outcomes and Treatments Associated with Head and Neck Cancer

Economic burden of acute myeloid leukemia: a literature review

Short- and long-term effects of acute myeloid leukemia on patient health-related quality of life

Economic burden of head and neck cancerA literature review

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