Orphanet Journal of Rare Diseases
Orphanet Journal of Rare Diseases > 2015 > 10 > 1 > 1-12
Orphanet Journal of Rare Diseases > 2015 > 10 > 1 > 1-22
Orphanet Journal of Rare Diseases > 2015 > 10 > 1 > 1-12
Orphanet Journal of Rare Diseases > 2015 > 10 > 1 > 1-22